Rare University
Recorded Sessions


Rare University is a new project that launched with the live stream of the 2016 RARE Patient Advocacy Summit. Formed as a partnership between Global Genes and PlatformQ Health, Rare University is dedicated to empowering anyone whose life has been impacted by a rare disease through clinically vetted medical education and advocacy resources. Learn more.

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Drug Dev Toolkit

From Molecules to Medicine: How Are New Drugs and Therapies Developed?

Today, more than ever before, the rare disease community can be optimistic about the development of new drug therapies. This Global Genes™ Toolkit walks you through how drugs are developed and approved in the U.S., the unique pathway for rare diseases, and how you can participate more effectively in the drug development process.

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Partners and Supporters

  • Global Genes
  • PlatformQ Health